STAT

OCTOBER 9, 2024

Newly published data show that seven out of 67 children who received Bluebird Bio’s gene therapy for a devastating neurological disorder in clinical trials have since gone on to develop blood cancers.  That means four additional patients have developed blood cancers since June 2022, when concerns about three cancer cases prompted the Food and Drug Administration to hold a hearing of outside advisers before approving the treatment, marketed as Skysona.

Hospitals 363

Hospitals 363

PharmaVoice

OCTOBER 9, 2024

Katelyn Jetelina, well known for her newsletter “Your Local Epidemiologist,” digs into the H5N1 outbreak, the public health response and what’s next for vaccinations.

Vaccines 306

Vaccines 306

STAT

OCTOBER 9, 2024

Two of the first efforts to treat Duchenne muscular dystrophy with CRISPR gene editing are getting off the ground in China, even as projects in the U.S. have seemingly stalled. Trials for the fatal muscle-wasting disease were started in the last couple of months by two different Chinese companies. One, GenAssist, has already dosed one young boy. Huidagene, the other biotech, expects to dose the first of three boys soon and report data by Q1 next year.

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PharmaVoice

OCTOBER 9, 2024

Small biotechs are making gains with AI drug development, and their advantages may help some push ahead without Big Pharma.

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Drug Development 211

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STAT

OCTOBER 9, 2024

LONDON — A trio of scientists who opened new doors in our understanding of the structure of proteins — the fundamental building blocks of biology — and even came up with ways to create new proteins won the Nobel Prize in chemistry Wednesday. The prize went to David Baker of the University of Washington, and to Demis Hassabis and John Jumper, who work at Google DeepMind in London.

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Pharmacy Is Right For Me

OCTOBER 9, 2024

Hello everyone, my name is Diana Martinez-Nava and I am a fourth-year student pharmacist at The University of New Mexico College of Pharmacy. I would like to take some time on this special month celebrating our Hispanic Heritage to share my story on my pharmacy journey. My interest in becoming a pharmacist began around the time I was 8 years old. I was that small child who could barely see over the counter at our neighborhood pharmacy next to my father’s arm who would be reaching out to collect,

Diabetes 130

Diabetes Community Pharmacies 130

Express Pharma

OCTOBER 9, 2024

Biocon Biologics, a global biosimilars company, has released the findings of a study focused on improving the adoption of biosimilars in low- and middle-income countries (LMICs). The study, commissioned by Biocon Biologics and developed in collaboration with Clarivate, highlights strategies to expand access to affordable healthcare solutions through biosimilars.

Biosimilars 101

Biosimilars Communication Diabetes 101

STAT

OCTOBER 9, 2024

WASHINGTON — A new report from congressional budget experts this week estimated that it would cost Medicare an additional $35 billion over nine years if the program began covering GLP-1 drugs for obesity. But the report also noted that half of seniors who would qualify for obesity coverage already have access to the drugs for other conditions.

Diabetes 326

Diabetes 326

Express Pharma

OCTOBER 9, 2024

In a crucial step forward, world leaders at the United Nations General Assembly (UNGA) have pledged to reduce antimicrobial resistance (AMR) associated fatalities by 10 per cent by 2030. This declaration, which emphasises a multi-sector approach, reflects a necessary shift toward a comprehensive “One Health” approach, integrating human, animal, and environmental health.

Vaccines 99

Vaccines 99

STAT

OCTOBER 9, 2024

In the last year, pharma incumbents have leaned into partnerships with AI-driven startups to supercharge drug discovery efforts. High-powered models of protein structure and molecule binding can help identify new disease targets, and even help design new drugs. But AI-derived or not, a new drug candidate still has to wind its way through the painstaking clinical trial process.

Drug Development 323

Drug Development 323

Speaker: Joe Sharpe and James Carlson

Payroll optimization can be one of the most time-consuming and complex factors of small business management. Yet, organizations that crack the code on streamlining employee compensation often discover innovative avenues for growth. With the right strategies in place, outsourcing and streamlining payroll processes can result in substantial time and resource savings.

Express Pharma

OCTOBER 9, 2024

Dr Jitendra Singh, Minister of State (I/C) of the Ministry of Science and Technology, Minister of State (I/C) of the Ministry of Earth Sciences, Minister of State in the Prime Minister’s Office, Minister of State in the Ministry of Personnel, Public Grievances and Pensions Minister of State in the Department of Atomic Energy and Minister of State in the Department of Space emphasised on India’s growing presence as a global hub for affordable, high-quality healthcare and medical tourism, which ha

Vaccines 93

Vaccines Process Improvement Biosimilars Immunization 93

STAT

OCTOBER 9, 2024

Machine-learning drug development company Insitro has inked three agreements with Eli Lilly for new medicines for metabolic diseases. But the deal is a little different compared to many recent deals between burgeoning artificial intelligence upstarts and established pharma giants: After identifying drug candidates, Insitro will be responsible for commercializing the drugs, and Lilly will be eligible for milestones and royalties.

Drug Development 309

Drug Development 309

BioPharma Dive

OCTOBER 9, 2024

Many pharma companies are now using de-identified lab data to identify potential patients and their physicians in time to impact the patient’s treatment plan. In this Q&A, learn how lab data can be used to increase patient access.

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STAT

OCTOBER 9, 2024

This story first appeared in The Readout newsletter.  Sign up for The Readout  and receive STAT’s award-winning biotech news delivered straight to your inbox.  Good morning to everyone except the Empire State Building.

Drug Pricing 278

Drug Pricing Drug Development 278

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pharmaphorum

OCTOBER 9, 2024

Sage Therapeutics stops development of dalzanemdor in Alzheimer's, a few months after pulling the plug on the drug in Parkinson's

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STAT

OCTOBER 9, 2024

After protracted legal battling, GSK has agreed to pay $2.2 billion to settle most of the pending lawsuits that claimed a discontinued version of the Zantac heartburn medication caused cancer. The settlement covers roughly 80,000 cases, or 93% of the suits that were outstanding in state courts around the U.S. At the same time, the company agreed to pay $70 million to settle a whistleblower lawsuit that was filed by Valisure, an independent laboratory that alleged GSK concealed the link between t

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The Pharmacist

OCTOBER 9, 2024

New national repeat prescribing guidance has been published in a bid to improve consistency and patient safety – and practice pharmacists have been described as 'well placed' to lead its implementation. The Royal Pharmaceutical Society (RPS) and the Royal College of GPs (RCGP) have this week launched a new repeat prescribing toolkit, in what is […] The post Practice pharmacists 'well placed' to lead on new repeat prescribing tool appeared first on The Pharmacist.

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STAT

OCTOBER 9, 2024

Good morning, everyone, and welcome to the middle of the week. Congratulations on making it this far, and remember there are only a few more days until the weekend arrives. So keep plugging away. After all, what are the alternatives? While you ponder the possibilities, we invite you to join us for a delightful cup of stimulation. Our choice today is crème brûlée.

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Speaker: Chris Antypas and Josh Halladay

Access to limited distribution drugs and payer contracts are key to pharmacy expansion. But how do you prepare your operations to take the next step? Meaningful data: Collect and share clinical data regarding outcomes, utilization, and more Reporting: Limited distribution models require efficient tracking and reporting systems Workflows: Align workflows with specific pharma and payer contractual requirements For in-depth, expert insights on pharmacy expansion, watch this webinar from Inovalon.

Drug Channels

OCTOBER 9, 2024

As regular readers of Drug Channels know, U.S. distribution and dispensing channels for prescription drugs are undergoing significant evolution and consolidation as the changing economics of pharmaceuticals challenge conventional business models. During this period of volatility, the core business model of the Big Three public pharmaceutical distribution companies—Cardinal Health, Cencora, and McKesson—remains intact.

Hospitals 87

Hospitals 87

STAT

OCTOBER 9, 2024

Another ultra-rare therapy will soon be subject to the gaze of an FDA advisory committee, with the fate of more than 200 boys diagnosed with Barth syndrome worldwide in the balance. On Thursday, the FDA cardiovascular and renal drugs advisory committee will be reviewing a new drug application for elamipretide hydrochloride injection , submitted by Stealth BioTherapeutics Inc., for the treatment of Barth syndrome.

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Drug Patent Watch

OCTOBER 9, 2024

The pharmaceutical industry plays a crucial role in global healthcare, providing essential medications that improve and save lives. Within this industry, generic pharmaceuticals are particularly important due to their affordability and accessibility.

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STAT

OCTOBER 9, 2024

Good morning, it’s Wednesday! A few of us at STAT thought yesterday might have been Wednesday, but no, it’s today. And in case you’re as confused as us, tomorrow is Thursday. (You would think editing a weekly podcast keeps me aware of what day it is, but you’d be wrong.) There are only 11 weeks left in 2024 … ! Anyway, the news: Chemistry Nobel goes to three scientists for protein discoveries Scientists who opened new doors in our understanding of the structure

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Pharmacy Management

pharmaphorum

OCTOBER 9, 2024

Ex-Pfizer CEO and finance chief withdraw support for Starboard Value campaign seeking a change in strategy at the pharma group.

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Pharmaceutical Technology

OCTOBER 9, 2024

City Therapeutics has announced its launch accompanied by a $135m Series A financing to lead advancements in RNAi-based medicine.

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pharmaphorum

OCTOBER 9, 2024

Zealand Pharma has suffered another setback in its bid to bring glucagon receptor agonist dasiglucagon for ultra-rare disease congenital hyperinsulinism (CHI) to the US market.For the second time in less than a year, the FDA has issued a complete response letter to the company citing the need for data on a third-party manufacturing site that had failed an earlier inspection by the agency.

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Express Pharma

OCTOBER 9, 2024

BizDateUp has led a USD 1 million pre-IPO funding round in Sorich, a pharmaceutical packaging startup. The funds will be used to optimise production, bolster working capital, and further develop patented products that meet necessary certifications. The investment will also help upgrade existing machinery, particularly for the production of high-margin items like Heat Transfer Labels (HTL).

Packaging 65

Packaging Labelling Compounding Pharmaceutical Companies 65

pharmaphorum

OCTOBER 9, 2024

Lilly names Thomas Fuchs as its first chief AI officer Phil.

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BioPharma Dive

OCTOBER 9, 2024

Thomas Fuchs will lead artificial intelligence initiatives across Lilly, including in drug discovery, clinical trials and manufacturing.

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PharmaTech

OCTOBER 9, 2024

Pharmaceutical Technology® Europe sat down with Hanns-Christian Mahler from ten23 health to discuss the fill/finish market and sustainability considerations for facilities.

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BioPharma Dive

OCTOBER 9, 2024

The company, which is building a database of biological interactions found in nature, revealed $60 million in funding and a collaboration with David Liu’s lab.

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Pharma Times

OCTOBER 9, 2024

New investment to advance gene therapies for kidney diseases

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Pharmaceutical Technology

OCTOBER 9, 2024

Ipsen has received the UK MHRA's approval for its Elafibranor (Iqirvo) for the treatment of primary biliary cholangitis (PBC) in adults.

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